Gene therapy using lentivirus to treat Wiskott-Aldrich Syndrome promising
The new research, led by researchers at the San Raffaele Telethon Institute for Gene Therapy in Milan, Italy was published in Science Express. The disorder that weakens the body’s immune system is caused by a mutation in a gene that encodes the protein WASP. The most often used therapy is a bone marrow or stem cell transplant from a matching donor — often a sibling or relative…